BBC Article Oct 2021: Gene silencing medicine transforms crippling pain

[Andy]

Quote:

An innovative type of medicine - called gene silencing - is set to be used on the NHS for people who live in crippling pain.

The drug treats acute intermittent porphyria, which runs in families and can leave people unable to work or have a normal life.

Clinical trials have shown severe symptoms were cut by 74% with the drug.

While porphyria is rare, experts say the field of gene silencing has the potential to revolutionise medicine.

https://www.bbc.co.uk/news/health-58988006

 

[Midnattsol]

"There's really nothing to stop us targeting so many different diseases from cancer to cardiovascular disease to cholesterol problems."

Except that many diseases have multiple problematic genes, and not all genes can be silenced as the protein they code for have other functions in the body not related to the disease. Still exciting though.